Barth syndrome

Ultra-rare disease

road through forest

Fierce Pharma

Stealth scores FDA approval for 1st Barth syndrome treatment

Stealth’s injection will be sold as Forzinity for Barth syndrome, an X-linked genetic disorder that weakens the heart and other muscles.

Gabrielle Masson Sep 19, 2025 6:00pm

accelerated

FDA aims for September approval decision for Stealth's drug

Aug 21, 2025 10:15am

question ask wonder who why

FDA denies request to reconsider Stealth's ultrarare disease med

Aug 8, 2025 1:58pm

FDA Adcomm

After agony, FDA adcomm favors Stealth's ultra-rare disease drug

Oct 10, 2024 6:20pm